Specific Delivery of MiRNA for High Efficient Inhibition of Prostate Cancer by RNA Nanotechnology
Peixuan Guo (Source: Molecular Therapy)
Source: Molecular Therapy - August 9, 2016 Category: Genetics & Stem Cells Authors: Daniel W Binzel Yi Shu Hui Li Meiyan Sun Qunshu Zhang Dan Shu Bin Guo Peixuan Guo Source Type: research

Complete Spectrum of CRISPR/Cas9-induced Mutations on HBV cccDNA
Sohn (Source: Molecular Therapy)
Source: Molecular Therapy - August 9, 2016 Category: Genetics & Stem Cells Authors: Christoph Seeger Ji A Sohn Source Type: research

In Vivo Selection Yields AAV-B1 Capsid for Central Nervous System and Muscle Gene Therapy
, Robert M Kotin, Douglas R Martin & Miguel Sena-Esteves (Source: Molecular Therapy)
Source: Molecular Therapy - August 9, 2016 Category: Genetics & Stem Cells Authors: Sourav R Choudhury Zachary Fitzpatrick Anne F Harris Stacy A Maitland Jennifer S Ferreira Yuanfan Zhang Shan Ma Rohit B Sharma Heather L Gray-Edwards Jacob A Johnson Aime K Johnson Laura C Alonso Claudio Punzo Kathryn R Wagner Casey A Maguire Robert M Kot Source Type: research

Development of Third-generation Cocal Envelope Producer Cell Lines for Robust Lentiviral Gene Transfer into Hematopoietic Stem Cells and T-cells
-Peter Kiem (Source: Molecular Therapy)
Source: Molecular Therapy - August 9, 2016 Category: Genetics & Stem Cells Authors: Olivier Humbert Don W. Gisch Martin E. Wohlfahrt Amie B. Adams Phil D. Greenberg Tom M. Schmitt Grant D. Trobridge Hans-Peter Kiem Source Type: research

Rapid and Efficient Stable Gene Transfer to Mesenchymal Stromal Cells Using a Modified Foamy Virus Vector
lga McClure (Source: Molecular Therapy)
Source: Molecular Therapy - August 9, 2016 Category: Genetics & Stem Cells Authors: Nathan Paul Sweeney Cathy Regan Jiahui Liu Antonio Galleu Francesco Dazzi Dirk Lindemann Charles Anthony Rupar Myra Olga McClure Source Type: research

Generation of Genetically Engineered Precursor T-Cells From Human Umbilical Cord Blood Using an Optimized Alpharetroviral Vector Platform
& Martin G Sauer (Source: Molecular Therapy)
Source: Molecular Therapy - August 9, 2016 Category: Genetics & Stem Cells Authors: Juwita H übner Shahabuddin S Hoseini Julia D Suerth Dirk Hoffmann Marcel Maluski Jessica Herbst Holger Maul Arnab Ghosh Britta Eiz-Vesper Qinggong Yuan Michael Ott Michael Heuser Axel Schambach Martin G Sauer Source Type: research

CRNDE Promotes Malignant Progression of Glioma by Attenuating miR-384/PIWIL4/STAT3 Axis
Yunhui Liu (Source: Molecular Therapy)
Source: Molecular Therapy - August 9, 2016 Category: Genetics & Stem Cells Authors: Jian Zheng Xiaobai Liu Ping Wang Yixue Xue Jun Ma Chengbin Qu Yunhui Liu Source Type: research

Safe and Efficient Gene Therapy for Pyruvate Kinase Deficiency
el Schambach, Shengfang Jin, Juan A Bueren, Eugenio Montini, Susana Navarro & Jose C Segovia (Source: Molecular Therapy)
Source: Molecular Therapy - August 9, 2016 Category: Genetics & Stem Cells Authors: Maria Garcia-Gomez Andrea Calabria Maria Garcia-Bravo Fabrizio Benedicenti Penelope Kosinski Sergio L ópez-Manzaneda Collin Hill Mar ía del Mar Mañu-Pereira Miguel A Mart ín Israel Orman Joan-LLuis Vives-Corrons Charles Kung Axel Schambach Shengfang J Source Type: research

Translational Implications for Off-the-shelf Immune Cells Expressing Chimeric Antigen Receptors
ooper (Source: Molecular Therapy)
Source: Molecular Therapy - August 9, 2016 Category: Genetics & Stem Cells Authors: Hiroki Torikai Laurence JN Cooper Source Type: research

Rethinking the Regulatory Infrastructure for Human Gene Transfer Clinical Trials
vid W Emery (Source: Molecular Therapy)
Source: Molecular Therapy - August 9, 2016 Category: Genetics & Stem Cells Authors: Christopher L Jenkins Mark L Bagarazzi Hans-Peter Kiem Arnold J Levine Dale Ando Carl H June Tony Reid David W Emery Source Type: research

Socializing Individualized T-Cell Cancer Immunotherapy
Molecular Therapy 24, 1170 (July 2016). doi:10.1038/mt.2016.132 Author: Richard G Vile (Source: Molecular Therapy)
Source: Molecular Therapy - August 9, 2016 Category: Genetics & Stem Cells Authors: Richard G Vile Source Type: research

The Role of Nonhuman Primate Animal Models in the Clinical Development of Pluripotent Stem Cell Therapies
ong Zou (Source: Molecular Therapy)
Source: Molecular Therapy - August 9, 2016 Category: Genetics & Stem Cells Authors: So Gun Hong Yongshun Lin Cynthia E Dunbar Jizhong Zou Source Type: research

Research Highlights
Molecular Therapy 24, 1164 (July 2016). doi:10.1038/mt.2016.130 (Source: Molecular Therapy)
Source: Molecular Therapy - August 9, 2016 Category: Genetics & Stem Cells Source Type: research

In This Issue
Molecular Therapy 24, 1163 (July 2016). doi:10.1038/mt.2016.129 (Source: Molecular Therapy)
Source: Molecular Therapy - August 9, 2016 Category: Genetics & Stem Cells Source Type: research

Expediting Viral Therapies For Cancers To the Clinic
Molecular Therapy 24, 1161 (July 2016). doi:10.1038/mt.2016.128 Author: Yuman Fong (Source: Molecular Therapy)
Source: Molecular Therapy - August 9, 2016 Category: Genetics & Stem Cells Authors: Yuman Fong Source Type: research