Nuclease Target Site Selection for Maximizing On-target Activity and Minimizing Off-target Effects in Genome Editing
; Gang Bao (Source: Molecular Therapy)
Source: Molecular Therapy - March 8, 2016 Category: Genetics & Stem Cells Authors: Ciaran M LeeThomas J CradickEli J FineGang Bao Source Type: research
Current Progress in Therapeutic Gene Editing for Monogenic Diseases
;ñez-Muñoz (Source: Molecular Therapy)
Source: Molecular Therapy - March 8, 2016 Category: Genetics & Stem Cells Authors: Versha PrakashMarc MooreRafael J Yáñez-Muñoz Source Type: research
Genome Engineering Using Adeno-associated Virus: Basic and Clinical Research Applications
Schaffer (Source: Molecular Therapy)
Source: Molecular Therapy - March 8, 2016 Category: Genetics & Stem Cells Authors: Thomas GajBenjamin E EpsteinDavid V Schaffer Source Type: research
Engineered Viruses as Genome Editing Devices
#231;alves (Source: Molecular Therapy)
Source: Molecular Therapy - March 8, 2016 Category: Genetics & Stem Cells Authors: Xiaoyu ChenManuel A F V Gonçalves Source Type: research
Genome-editing Technologies for Gene and Cell Therapy
rsbach (Source: Molecular Therapy)
Source: Molecular Therapy - March 8, 2016 Category: Genetics & Stem Cells Authors: Morgan L MaederCharles A Gersbach Source Type: research
Salient Features of Endonuclease Platforms for Therapeutic Genome Editing
Morgan (Source: Molecular Therapy)
Source: Molecular Therapy - March 8, 2016 Category: Genetics & Stem Cells Authors: Michael T CertoRichard A Morgan Source Type: research
Patent Law and Genome Engineering: A Short Guide to a Rapidly Changing Landscape
Molecular Therapy 24,
419 (March 2016). doi:10.1038/mt.2016.31
Author: Ross Cloney (Source: Molecular Therapy)
Source: Molecular Therapy - March 8, 2016 Category: Genetics & Stem Cells Authors: Ross Cloney Source Type: research
A CRISPR Approach for Reactivating Latent HIV-1
Klase (Source: Molecular Therapy)
Source: Molecular Therapy - March 8, 2016 Category: Genetics & Stem Cells Authors: Angel LinZachary Klase Source Type: research
CRISPR/Cas9 Flexes Its Muscles: In Vivo Somatic Gene Editing for Muscular Dystrophy
Chuah (Source: Molecular Therapy)
Source: Molecular Therapy - March 8, 2016 Category: Genetics & Stem Cells Authors: Thierry VandenDriesscheMarinee K Chuah Source Type: research
A Perspective on the State of Genome Editing
Molecular Therapy 24,
412 (March 2016). doi:10.1038/mt.2016.28
Author: Dana Carroll (Source: Molecular Therapy)
Source: Molecular Therapy - March 8, 2016 Category: Genetics & Stem Cells Authors: Dana Carroll Source Type: research
Research Highlights
Molecular Therapy 24,
411 (March 2016). doi:10.1038/mt.2016.27 (Source: Molecular Therapy)
Source: Molecular Therapy - March 8, 2016 Category: Genetics & Stem Cells Source Type: research
In This Issue
Molecular Therapy 24,
410 (March 2016). doi:10.1038/mt.2016.26 (Source: Molecular Therapy)
Source: Molecular Therapy - March 8, 2016 Category: Genetics & Stem Cells Source Type: research
A New Induction to the Gene and Cell Therapy Hall Of Fame: Genome Editing
Molecular Therapy 24,
407 (March 2016). doi:10.1038/mt.2016.25
Author: Michel Sadelain (Source: Molecular Therapy)
Source: Molecular Therapy - March 8, 2016 Category: Genetics & Stem Cells Authors: Michel Sadelain Source Type: research
Variable Virulence and Efficacy of BCG Vaccine Strains in Mice and Correlation With Genome Polymorphisms
ng-xia Lin & Jun Liu (Source: Molecular Therapy)
Source: Molecular Therapy - February 24, 2016 Category: Genetics & Stem Cells Authors: Lu ZhangHuan-wei RuFu-zeng ChenChun-yan JinRui-feng SunXiao-yong FanMing GuoJun-tao MaiWen-xi XuQing-xia LinJun Liu Source Type: research
Genetic Immunization With In Vivo Dendritic Cell-targeting Liposomal DNA Vaccine Carrier Induces Long-lasting Antitumor Immune Response
Chaudhuri (Source: Molecular Therapy)
Source: Molecular Therapy - February 24, 2016 Category: Genetics & Stem Cells Authors: Arup GaruGopikrishna MokuSuresh Kumar GullaArabinda Chaudhuri Source Type: research