In This Issue
Molecular Therapy 24,
1886 (November 2016). doi:10.1038/mt.2016.189 (Source: Molecular Therapy)
Source: Molecular Therapy - December 4, 2016 Category: Genetics & Stem Cells Source Type: research
Eteplirsen Approved for Duchenne Muscular Dystrophy: The FDA Faces a Difficult Choice
Molecular Therapy 24,
1884 (November 2016). doi:10.1038/mt.2016.188
Author: Cy A Stein (Source: Molecular Therapy)
Source: Molecular Therapy - December 4, 2016 Category: Genetics & Stem Cells Authors: Cy A Stein Source Type: research
The EMA Framework of Collaboration With Academic Stakeholders
accio (Source: Molecular Therapy)
Source: Molecular Therapy - December 4, 2016 Category: Genetics & Stem Cells Authors: Anton Ussi Giovanni Migliaccio Source Type: research
Corrigendum to “Inducible HGF-secreting Human Umbilical Cord Blood-derived MSCs Produced via TALEN-mediated Genome Editing Promoted Angiogenesis”
Corrigendum to “Inducible HGF-secreting Human Umbilical Cord Blood-derived MSCs Produced via TALEN-mediated Genome Editing Promoted Angiogenesis”
Molecular Therapy 24,
1881 (October 2016). doi:10.1038/mt.2016.176 (Source: Molecular Therapy)
Source: Molecular Therapy - November 6, 2016 Category: Genetics & Stem Cells Source Type: research
Lentiviral Vector Gene Therapy Protects XCGD Mice From Acute Staphylococcus aureus Pneumonia and Inflammatory Response
Alessandro Aiuti (Source: Molecular Therapy)
Source: Molecular Therapy - November 6, 2016 Category: Genetics & Stem Cells Authors: Giada Farinelli Raisa Jofra Hernandez Alice Rossi Serena Ranucci Francesca Sanvito Maddalena Migliavacca Chiara Brombin Aleksandar Pramov Clelia Di Serio Chiara Bovolenta Bernhard Gentner Alessandra Bragonzi Alessandro Aiuti Source Type: research
Mesenchymal Stromal Cells Mitigate Experimental Colitis via Insulin-like Growth Factor Binding Protein 7-mediated Immunosuppression
ndy Peng Xiang (Source: Molecular Therapy)
Source: Molecular Therapy - November 6, 2016 Category: Genetics & Stem Cells Authors: Yan Liao Junxia Lei Muyun Liu Wanwen Lin Dongxi Hong Ying Tuo Mei Hua Jiang Huimin Xia Maosheng Wang Weijun Huang Andy Peng Xiang Source Type: research
MiR-29a Assists in Preventing the Activation of Human Stellate Cells and Promotes Recovery From Liver Fibrosis in Mice
Murakami (Source: Molecular Therapy)
Source: Molecular Therapy - November 6, 2016 Category: Genetics & Stem Cells Authors: Yoshinari Matsumoto Saori Itami Masahiko Kuroda Katsutoshi Yoshizato Norifumi Kawada Yoshiki Murakami Source Type: research
Exosome-mediated Delivery of Hydrophobically Modified siRNA for Huntingtin mRNA Silencing
mp; Anastasia Khvorova (Source: Molecular Therapy)
Source: Molecular Therapy - November 6, 2016 Category: Genetics & Stem Cells Authors: Marie-C écile Didiot Lauren M Hall Andrew H Coles Reka A Haraszti Bruno MDC Godinho Kathryn Chase Ellen Sapp Socheata Ly Julia F Alterman Matthew R Hassler Dimas Echeverria Lakshmi Raj David V Morrissey Marian DiFiglia Neil Aronin Anastasia Khvorova Source Type: research
Strand and Cell Type-specific Function of microRNA-126 in Angiogenesis
sheng Wang (Source: Molecular Therapy)
Source: Molecular Therapy - November 6, 2016 Category: Genetics & Stem Cells Authors: Qinbo Zhou Chastain Anderson Jakub Hanus Fangkun Zhao Jing Ma Akihiko Yoshimura Shusheng Wang Source Type: research
Role of HCP5-miR-139-RUNX1 Feedback Loop in Regulating Malignant Behavior of Glioma Cells
; Yunhui Liu (Source: Molecular Therapy)
Source: Molecular Therapy - November 6, 2016 Category: Genetics & Stem Cells Authors: Hao Teng Ping Wang Yixue Xue Xiaobai Liu Jun Ma Heng Cai Zhuo Xi Zhen Li Yunhui Liu Source Type: research
Somatic Therapy of a Mouse SMA Model with a U7 snRNA Gene Correcting SMN2 Splicing
Schümperli (Source: Molecular Therapy)
Source: Molecular Therapy - November 6, 2016 Category: Genetics & Stem Cells Authors: Philipp Odermatt Judith Tr üb Lavinia Furrer Roger Fricker Andreas Marti Daniel Sch ümperli Source Type: research
Edible Ginger-derived Nano-lipids Loaded with Doxorubicin as a Novel Drug-delivery Approach for Colon Cancer Therapy
dier Merlin (Source: Molecular Therapy)
Source: Molecular Therapy - November 6, 2016 Category: Genetics & Stem Cells Authors: Mingzhen Zhang Bo Xiao Huan Wang Moon Kwon Han Zhan Zhang Emilie Viennois Changlong Xu Didier Merlin Source Type: research
Integrated Safety Assessment of 2 ′-O-Methoxyethyl Chimeric Antisense Oligonucleotides in NonHuman Primates and Healthy Human Volunteers
Integrated Safety Assessment of 2′-O-Methoxyethyl Chimeric Antisense Oligonucleotides in NonHuman Primates and Healthy Human Volunteers
Molecular Therapy 24,
1771 (October 2016). doi:10.1038/mt.2016.136
Authors: Stanley T Crooke, Brenda F Baker, T Jesse Kwoh, Wei Cheng, Dan J Schulz, Shuting Xia, Nelson Salgado, Huynh-Hoa Bui, Christopher E Hart, Sebastien A Burel, Husam S Younis, Richard S Geary, Scott P Henry & Sanjay Bhanot (Source: Molecular Therapy)
Source: Molecular Therapy - November 6, 2016 Category: Genetics & Stem Cells Authors: Stanley T Crooke Brenda F Baker T Jesse Kwoh Wei Cheng Dan J Schulz Shuting Xia Nelson Salgado Huynh-Hoa Bui Christopher E Hart Sebastien A Burel Husam S Younis Richard S Geary Scott P Henry Sanjay Bhanot Source Type: research
Extracellular Antibody Drug Conjugates Exploiting the Proximity of Two Proteins
James R Prudent (Source: Molecular Therapy)
Source: Molecular Therapy - November 6, 2016 Category: Genetics & Stem Cells Authors: David J Marshall Scott S Harried John L Murphy Chad A Hall Mohammed S Shekhani Christophe Pain Conner A Lyons Antonella Chillemi Fabio Malavasi Homer L Pearce Jon S Thorson James R Prudent Source Type: research
The Retinoid Agonist Tazarotene Promotes Angiogenesis and Wound Healing
hattacharya (Source: Molecular Therapy)
Source: Molecular Therapy - November 6, 2016 Category: Genetics & Stem Cells Authors: Ayman Al Haj Zen Dorota A Nawrot Alison Howarth Andrea Caporali Daniel Ebner Aude Vernet Jurgen E Schneider Shoumo Bhattacharya Source Type: research
