Evaluation of AAV-mediated Gene Therapy for Central Nervous System Disease in Canine Mucopolysaccharidosis VII
ping Gao, James M Wilson, Margret Casal, Katherine P Ponder & Mark E Haskins (Source: Molecular Therapy)
Source: Molecular Therapy - February 24, 2016 Category: Genetics & Stem Cells Authors: Brittney L GurdaAdrien De Guilhem De LatailladePeter BellYanqing ZhuHongwei YuPing WangJessica BagelCharles H ViteTracey SikoraChristian HindererRoberto CalcedoAlexander D YoxRichard A SteetTherese RuanePatricia O'DonnellGuangping GaoJames M WilsonMargret Source Type: research

Under Pressure: Elevated Blood Pressure Enhances Targeting of Tumors by Oncolytic Viruses
Fisher (Source: Molecular Therapy)
Source: Molecular Therapy - February 24, 2016 Category: Genetics & Stem Cells Authors: Leonard W SeymourKerry D Fisher Source Type: research

The BCG Strain Pool: Diversity Matters
Brosch (Source: Molecular Therapy)
Source: Molecular Therapy - February 24, 2016 Category: Genetics & Stem Cells Authors: Daria BottaiRoland Brosch Source Type: research

Genotoxicity in Mice Following AAV Gene Delivery: A Safety Concern for Human Gene Therapy?
s P Venditti (Source: Molecular Therapy)
Source: Molecular Therapy - February 24, 2016 Category: Genetics & Stem Cells Authors: Randy J ChandlerMatthew C LaFaveGaurav K VarshneyShawn M BurgessCharles P Venditti Source Type: research

Research Highlights
Molecular Therapy 24, 197 (February 2016). doi:10.1038/mt.2016.16 (Source: Molecular Therapy)
Source: Molecular Therapy - February 24, 2016 Category: Genetics & Stem Cells Source Type: research

In This Issue
Molecular Therapy 24, 196 (February 2016). doi:10.1038/mt.2016.15 (Source: Molecular Therapy)
Source: Molecular Therapy - February 24, 2016 Category: Genetics & Stem Cells Source Type: research

New Momentum for the Field of Oligonucleotide Therapeutics
Molecular Therapy 24, 193 (February 2016). doi:10.1038/mt.2016.14 Author: Annemieke Aartsma-Rus (Source: Molecular Therapy)
Source: Molecular Therapy - February 24, 2016 Category: Genetics & Stem Cells Authors: Annemieke Aartsma-Rus Source Type: research

The Role of Neutrophils in Measles Virus–mediated Oncolysis Differs Between B-cell Malignancies and Is Not Always Enhanced by GCSF
The Role of Neutrophils in Measles Virus–mediated Oncolysis Differs Between B-cell Malignancies and Is Not Always Enhanced by GCSF Molecular Therapy 24, 184 (January 2016). doi:10.1038/mt.2015.149 Authors: Aditi Dey, Yu Zhang, Anna Z Castleton, Katharine Bailey, Brendan Beaton, Bella Patel & Adele K Fielding (Source: Molecular Therapy)
Source: Molecular Therapy - February 8, 2016 Category: Genetics & Stem Cells Authors: Aditi DeyYu ZhangAnna Z CastletonKatharine BaileyBrendan BeatonBella PatelAdele K Fielding Source Type: research

Chronic Activation of Innate Immunity Correlates With Poor Prognosis in Cancer Patients Treated With Oncolytic Adenovirus
nder, Timo Joensuu, Johan Lundin & Akseli Hemminki (Source: Molecular Therapy)
Source: Molecular Therapy - February 8, 2016 Category: Genetics & Stem Cells Authors: Kristian TaipaleIlkka LiikanenJuuso JuhilaRiku TurkkiSiri TähtinenMatti KankainenLotta VassilevAri RistimäkiAnniina KoskiAnna KanervaIulia DiaconuVincenzo CerulloMarkus Vähä-KoskelaMinna OksanenNina LinderTimo JoensuuJohan LundinAkseli Hemminki Source Type: research

Combination Therapy With Reovirus and Anti-PD-1 Blockade Controls Tumor Growth Through Innate and Adaptive Immune Responses
n Melcher & Richard Vile (Source: Molecular Therapy)
Source: Molecular Therapy - February 8, 2016 Category: Genetics & Stem Cells Authors: Karishma RajaniChristopher ParrishTimothy KottkeJill ThompsonShane ZaidiLiz IlettKevin G ShimRosa-Maria DiazHardev PandhaKevin HarringtonMatt CoffeyAlan MelcherRichard Vile Source Type: research

Activation of Cyclic Adenosine Monophosphate Pathway Increases the Sensitivity of Cancer Cells to the Oncolytic Virus M1
ping Gao, Phillip W L Tai, Jun Hu & Guangmei Yan (Source: Molecular Therapy)
Source: Molecular Therapy - February 8, 2016 Category: Genetics & Stem Cells Authors: Kai LiHaipeng ZhangJianguang QiuYuan LinJiankai LiangXiao XiaoLiwu FuFang WangJing CaiYaqian TanWenbo ZhuWei YinBingzheng LuFan XingLipeng TangMin YanJialuo MaiYuan LiWenli ChenPengxin QiuXingwen SuGuangping GaoPhillip W L TaiJun HuGuangmei Yan Source Type: research

Delivery of siRNAs to Dendritic Cells Using DEC205-Targeted Lipid Nanoparticles to Inhibit Immune Responses
; Deborah Palliser (Source: Molecular Therapy)
Source: Molecular Therapy - February 8, 2016 Category: Genetics & Stem Cells Authors: Joseph A KatakowskiGayatri MukherjeeSamantha E WilnerKeith E MaierMichael Travis HarrisonTeresa P DiLorenzoMatthew LevyDeborah Palliser Source Type: research

An RNA Molecule Derived From Sendai Virus DI Particles Induces Antitumor Immunity and Cancer Cell-selective Apoptosis
i Kaneda (Source: Molecular Therapy)
Source: Molecular Therapy - February 8, 2016 Category: Genetics & Stem Cells Authors: Li-Wen LiuTomoyuki NishikawaYasufumi Kaneda Source Type: research

Kidney-specific Sonoporation-mediated Gene Transfer
& Satoshi Gojo (Source: Molecular Therapy)
Source: Molecular Therapy - February 8, 2016 Category: Genetics & Stem Cells Authors: Ryo IshidaDaisuke KamiTetsuro KusabaYuhei KiritaTsunao KishidaOsam MazdaTakaomi AdachiSatoshi Gojo Source Type: research

Directed Alternative Splicing in Nijmegen Breakage Syndrome: Proof of Principle Concerning Its Therapeutical Application
Sperling & Martin Digweed (Source: Molecular Therapy)
Source: Molecular Therapy - February 8, 2016 Category: Genetics & Stem Cells Authors: Bastian SalewskyGabriele HildebrandSusanne RotheAnn Christin ParplysJanina RadszewskiMoritz KieslichPetra WessendorfHarald KrenzlinKerstin BorgmannAndré NussenzweigKarl SperlingMartin Digweed Source Type: research