Evaluation of AAV-mediated Gene Therapy for Central Nervous System Disease in Canine Mucopolysaccharidosis VII

Evaluation of AAV-mediated Gene Therapy for Central Nervous System Disease in Canine Mucopolysaccharidosis VII Molecular Therapy 24, 206 (February 2016). doi:10.1038/mt.2015.189 Authors: Brittney L Gurda, Adrien De Guilhem De Lataillade, Peter Bell, Yanqing Zhu, Hongwei Yu, Ping Wang, Jessica Bagel, Charles H Vite, Tracey Sikora, Christian Hinderer, Roberto Calcedo, Alexander D Yox, Richard A Steet, Therese Ruane, Patricia O'Donnell, Guangping Gao, James M Wilson, Margret Casal, Katherine P Ponder & Mark E Haskins
Source: Molecular Therapy - Category: Genetics & Stem Cells Authors: Source Type: research
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