ASGCT 19th Annual Meeting: Program
Molecular Therapy 24, i (April 2016). doi:10.1038/mt.2016.77 (Source: Molecular Therapy)
Source: Molecular Therapy - April 21, 2016 Category: Genetics & Stem Cells Source Type: research

Corrigendum to “PTH Induces Systemically Administered Mesenchymal Stem Cells to Migrate to and Regenerate Spine Injuries”
Corrigendum to “PTH Induces Systemically Administered Mesenchymal Stem Cells to Migrate to and Regenerate Spine Injuries” Molecular Therapy 24, 843 (April 2016). doi:10.1038/mt.2016.59 (Source: Molecular Therapy)
Source: Molecular Therapy - April 14, 2016 Category: Genetics & Stem Cells Source Type: research

Corrigendum to “Development of Nonviral Vectors Targeting the Brain as a Therapeutic Approach For Parkinson’s Disease and Other Brain Disorders”
Corrigendum to “Development of Nonviral Vectors Targeting the Brain as a Therapeutic Approach For Parkinson’s Disease and Other Brain Disorders” Molecular Therapy 24, 843 (April 2016). doi:10.1038/mt.2016.58 Author: (Source: Molecular Therapy)
Source: Molecular Therapy - April 14, 2016 Category: Genetics & Stem Cells Source Type: research

Novel Conserved-region T-cell Mosaic Vaccine With High Global HIV-1 Coverage Is Recognized by Protective Responses in Untreated Infection
rber & Tomáš Hanke (Source: Molecular Therapy)
Source: Molecular Therapy - April 14, 2016 Category: Genetics & Stem Cells Authors: Beatrice OndondoHayato MurakoshiGenevieve CluttonSultan Abdul-JawadEdmund G-T WeeHiroyuki GatanagaShinichi OkaAndrew J McMichaelMasafumi TakiguchiBette KorberTomáš Hanke Source Type: research

Serial Activation of the Inducible Caspase 9 Safety Switch After Human Stem Cell Transplantation
olm K. Brenner (Source: Molecular Therapy)
Source: Molecular Therapy - April 14, 2016 Category: Genetics & Stem Cells Authors: Xiaoou ZhouSwati NaikOlga DakhovaGianpietro DottiHelen E. HeslopMalcolm K. Brenner Source Type: research

Functional Restoration of gp91phox-Oxidase Activity by BAC Transgenesis and Gene Targeting in X-linked Chronic Granulomatous Disease iPSCs
& Konstantinos Anastassiadis (Source: Molecular Therapy)
Source: Molecular Therapy - April 14, 2016 Category: Genetics & Stem Cells Authors: Magdalena LaugschMaria RostovskayaSergiy VelychkoCornelia RichterAriane ZimmerBarbara KlinkEvelin SchröckMichael HaaseKatrin NeumannSebastian ThiemeJoachim RoeslerSebastian BrennerKonstantinos Anastassiadis Source Type: research

Human Mesenchymal Stem Cell Delivery System Modulates Ischemic Cardiac Remodeling With an Increase of Coronary Artery Blood Flow
ng Wan Kim (Source: Molecular Therapy)
Source: Molecular Therapy - April 14, 2016 Category: Genetics & Stem Cells Authors: Young Sook LeeWan Seok JooHyun Soo KimSung Wan Kim Source Type: research

Actin-resistant DNAse I Expression From Oncolytic Adenovirus Enadenotucirev Enhances Its Intratumoral Spread and Reduces Tumor Growth
rry D Fisher (Source: Molecular Therapy)
Source: Molecular Therapy - April 14, 2016 Category: Genetics & Stem Cells Authors: Alison TedcastleSam IllingworthAlice BrownLeonard W SeymourKerry D Fisher Source Type: research

Relationship Between the Physicochemical Properties of Lipid Nanoparticles and the Quality of siRNA Delivery to Liver Cells
Harashima (Source: Molecular Therapy)
Source: Molecular Therapy - April 14, 2016 Category: Genetics & Stem Cells Authors: Yusuke SatoHiroto HatakeyamaMamoru HyodoHideyoshi Harashima Source Type: research

Smooth Muscle Cell–targeted RNA Aptamer Inhibits Neointimal Formation
Smooth Muscle Cell–targeted RNA Aptamer Inhibits Neointimal Formation Molecular Therapy 24, 779 (April 2016). doi:10.1038/mt.2015.235 Authors: William H Thiel, Carla L Esposito, David D Dickey, Justin P Dassie, Matthew E Long, Joshua Adam, Jennifer Streeter, Brandon Schickling, Maysam Takapoo, Katie S Flenker, Julia Klesney-Tait, Vittorio de Franciscis, Francis J Miller & Paloma H Giangrande (Source: Molecular Therapy)
Source: Molecular Therapy - April 14, 2016 Category: Genetics & Stem Cells Authors: William H ThielCarla L EspositoDavid D DickeyJustin P DassieMatthew E LongJoshua AdamJennifer StreeterBrandon SchicklingMaysam TakapooKatie S FlenkerJulia Klesney-TaitVittorio de FranciscisFrancis J MillerPaloma H Giangrande Source Type: research

Inhibition of Glycolate Oxidase With Dicer-substrate siRNA Reduces Calcium Oxalate Deposition in a Mouse Model of Primary Hyperoxaluria Type 1
, Henryk Dudek, Eduardo Salido, Bob D Brown & Chengjung Lai (Source: Molecular Therapy)
Source: Molecular Therapy - April 14, 2016 Category: Genetics & Stem Cells Authors: Chaitali DuttaNicole Avitahl-CurtisNatalie PursellMarita Larsson CohenBenjamin HolmesRohan DiwanjiWei ZhouLuciano ApponiMartin KoserBo YingDongyu ChenXue ShuiUtsav SaxenaWendy A CyrAnee ShahNaim NazefWeimin WangMarc AbramsHenryk DudekEduardo SalidoBob D B Source Type: research

Combination wt-p53 and MicroRNA-125b Transfection in a Genetically Engineered Lung Cancer Model Using Dual CD44/EGFR-targeting Nanoparticles
Mansoor M Amiji (Source: Molecular Therapy)
Source: Molecular Therapy - April 14, 2016 Category: Genetics & Stem Cells Authors: Meghna TalekarMalav TrivediParin ShahQijun OuyangAdwait OkaSrujan GandhamMansoor M Amiji Source Type: research

Development of Nonviral Vectors Targeting the Brain as a Therapeutic Approach For Parkinson’s Disease and Other Brain Disorders
Development of Nonviral Vectors Targeting the Brain as a Therapeutic Approach For Parkinson’s Disease and Other Brain Disorders Molecular Therapy 24, 746 (April 2016). doi:10.1038/mt.2015.232 Authors: Hayate Javed, Sindhu A Menon, Karima M Al-Mansoori, Abdelmojib Al-Wandi, Nour K Majbour, Mustafa T Ardah, Shiji Varghese, Nishant N Vaikath, M Emdadul Haque, Mimoun Azzouz & Omar MA El-Agnaf (Source: Molecular Therapy)
Source: Molecular Therapy - April 14, 2016 Category: Genetics & Stem Cells Authors: Hayate JavedSindhu A MenonKarima M Al-MansooriAbdelmojib Al-WandiNour K MajbourMustafa T ArdahShiji VargheseNishant N VaikathM Emdadul HaqueMimoun AzzouzOmar MA El-Agnaf Source Type: research

Clonal Dynamics In Vivo of Virus Integration Sites of T Cells Expressing a Safety Switch
mp; Gianpietro Dotti (Source: Molecular Therapy)
Source: Molecular Therapy - April 14, 2016 Category: Genetics & Stem Cells Authors: Edmund C ChangHao LiuJohn A WestXiaoou ZhouOlga DakhovaDavid A WheelerHelen E HeslopMalcolm K BrennerGianpietro Dotti Source Type: research

Widespread Central Nervous System Gene Transfer and Silencing After Systemic Delivery of Novel AAV-AS Vector
ping Gao & Miguel Sena-Esteves (Source: Molecular Therapy)
Source: Molecular Therapy - April 14, 2016 Category: Genetics & Stem Cells Authors: Sourav R ChoudhuryAnne F HarrisDamien J CabralAllison M KeelerEllen SappJennifer S FerreiraHeather L Gray-EdwardsJacob A JohnsonAime K JohnsonQin SuLorelei StoicaMarian DiFigliaNeil AroninDouglas R MartinGuangping GaoMiguel Sena-Esteves Source Type: research