CD123-Engager T Cells as a Novel Immunotherapeutic for Acute Myeloid Leukemia
phen Gottschalk (Source: Molecular Therapy)
Source: Molecular Therapy - September 28, 2016 Category: Genetics & Stem Cells Authors: Challice L Bonifant Arpad Szoor David Torres Nicholos Joseph Mireya Paulina Velasquez Kota Iwahori Amos Gaikwad Phuong Nguyen Caroline Arber Xiao-Tong Song Michele Redell Stephen Gottschalk Source Type: research
Feasibility and Safety of RNA-transfected CD20-specific Chimeric Antigen Receptor T Cells in Dogs with Spontaneous B Cell Lymphoma
icola J Mason (Source: Molecular Therapy)
Source: Molecular Therapy - September 28, 2016 Category: Genetics & Stem Cells Authors: M Kazim Panjwani Jenessa B Smith Keith Schutsky Josephine Gnanandarajah Colleen M O ’Connor Daniel J Powell Nicola J Mason Source Type: research
Optimization of Morpholino Antisense Oligonucleotides Targeting the Intronic Repressor Element1 in Spinal Muscular Atrophy
tian L Lorson (Source: Molecular Therapy)
Source: Molecular Therapy - September 28, 2016 Category: Genetics & Stem Cells Authors: Erkan Y Osman Charles W Washington Kevin A Kaifer Chiara Mazzasette Teresa N Patitucci Kyra M Florea Madeline E Simon Chien-Ping Ko Allison D Ebert Christian L Lorson Source Type: research
Advanced Design of Dumbbell-shaped Genetic Minimal Vectors Improves Non-coding and Coding RNA Expression
Volker Patzel (Source: Molecular Therapy)
Source: Molecular Therapy - September 28, 2016 Category: Genetics & Stem Cells Authors: Xiaoou Jiang Han Yu Cui Rong Teo Genim Siu Xian Tan Sok Chin Goh Parasvi Patel Yiqiang Kevin Chua Nasirah Banu Sahul Hameed Antonio Bertoletti Volker Patzel Source Type: research
High Efficiency CRISPR/Cas9-mediated Gene Editing in Primary Human T-cells Using Mutant Adenoviral E4orf6/E1b55k “Helper” Proteins
High Efficiency CRISPR/Cas9-mediated Gene Editing in Primary Human T-cells Using Mutant Adenoviral E4orf6/E1b55k “Helper” Proteins
Molecular Therapy 24,
1570 (september 2016). doi:10.1038/mt.2016.105
Authors: Kamila S Gwiazda, Alexandra E Grier, Jaya Sahni, Stephen M Burleigh, Unja Martin, Julia G Yang, Nicholas A Popp, Michelle C Krutein, Iram F Khan, Kyle Jacoby, Michael C Jensen, David J Rawlings & Andrew M Scharenberg (Source: Molecular Therapy)
Source: Molecular Therapy - September 28, 2016 Category: Genetics & Stem Cells Authors: Kamila S Gwiazda Alexandra E Grier Jaya Sahni Stephen M Burleigh Unja Martin Julia G Yang Nicholas A Popp Michelle C Krutein Iram F Khan Kyle Jacoby Michael C Jensen David J Rawlings Andrew M Scharenberg Source Type: research
CRISPR/Cas9-Mediated Correction of the Sickle Mutation in Human CD34+ cells
ni, Roger P Hollis & Donald B Kohn (Source: Molecular Therapy)
Source: Molecular Therapy - September 28, 2016 Category: Genetics & Stem Cells Authors: Megan D Hoban Dianne Lumaquin Caroline Y Kuo Zulema Romero Joseph Long Michelle Ho Courtney S Young Michelle Mojadidi Sorel Fitz-Gibbon Aaron R Cooper Georgia R Lill Fabrizia Urbinati Beatriz Campo-Fernandez Carmen F Bjurstrom Matteo Pellegrini Roger P Ho Source Type: research
Anti-apoptotic Effects of Human Wharton ’s Jelly-derived Mesenchymal Stem Cells on Skeletal Muscle Cells Mediated via Secretion of XCL1
Anti-apoptotic Effects of Human Wharton’s Jelly-derived Mesenchymal Stem Cells on Skeletal Muscle Cells Mediated via Secretion of XCL1
Molecular Therapy 24,
1550 (september 2016). doi:10.1038/mt.2016.125
Authors: SooJin Kwon, Soo Mi Ki, Sang Eon Park, Min-Jeong Kim, Brian Hyung, Na Kyung Lee, Sangmi Shim, Byung-Ok Choi, Duk L Na, Ji Eun Lee & Jong Wook Chang (Source: Molecular Therapy)
Source: Molecular Therapy - September 28, 2016 Category: Genetics & Stem Cells Authors: SooJin Kwon Soo Mi Ki Sang Eon Park Min-Jeong Kim Brian Hyung Na Kyung Lee Sangmi Shim Byung-Ok Choi Duk L Na Ji Eun Lee Jong Wook Chang Source Type: research
In Situ Pluripotency Factor Expression Promotes Functional Recovery From Cerebral Ischemia
ung-Rae Cho (Source: Molecular Therapy)
Source: Molecular Therapy - September 28, 2016 Category: Genetics & Stem Cells Authors: Jung Hwa Seo Min-Young Lee Ji Hea Yu Myung-Sun Kim Myungjae Song Cheong Hoon Seo Hyongbum (Henry) Kim Sung-Rae Cho Source Type: research
Development of an Attenuated Tat Protein as a Highly-effective Agent to Specifically Activate HIV-1 Latency
ng Cai & Hui Zhang (Source: Molecular Therapy)
Source: Molecular Therapy - September 28, 2016 Category: Genetics & Stem Cells Authors: Guannan Geng Bingfeng Liu Cancan Chen Kang Wu Jun Liu Yijun Zhang Ting Pan Jun Li Yue Yin Junsong Zhang Feng Huang Fei Yu Jingliang Chen Xiancai Ma Jie Zhou Ersheng Kuang Chao Liu Weiping Cai Hui Zhang Source Type: research
Viral and Synthetic RNA Vector Technologies and Applications
hambach (Source: Molecular Therapy)
Source: Molecular Therapy - September 28, 2016 Category: Genetics & Stem Cells Authors: Juliane W Schott Michael Morgan Melanie Galla Axel Schambach Source Type: research
Man ’s Best Friend: Utilizing Naturally Occurring Tumors in Dogs to Improve Chimeric Antigen Receptor T-cell Therapy for Human Cancers
Man’s Best Friend: Utilizing Naturally Occurring Tumors in Dogs to Improve Chimeric Antigen Receptor T-cell Therapy for Human Cancers
Molecular Therapy 24,
1511 (september 2016). doi:10.1038/mt.2016.173
Authors: Melinda Mata & Stephen Gottschalk (Source: Molecular Therapy)
Source: Molecular Therapy - September 28, 2016 Category: Genetics & Stem Cells Authors: Melinda Mata Stephen Gottschalk Source Type: research
A Self-restricted CRISPR System to Reduce Off-target Effects
Qiurong Ding (Source: Molecular Therapy)
Source: Molecular Therapy - September 28, 2016 Category: Genetics & Stem Cells Authors: Yanhao Chen Xiaojian Liu Yongxian Zhang Hui Wang Hao Ying Mingyao Liu Dali Li Kathy O Lui Qiurong Ding Source Type: research
Research Highlights
Molecular Therapy 24,
1507 (september 2016). doi:10.1038/mt.2016.171 (Source: Molecular Therapy)
Source: Molecular Therapy - September 28, 2016 Category: Genetics & Stem Cells Source Type: research
In This Issue
Molecular Therapy 24,
1506 (september 2016). doi:10.1038/mt.2016.170 (Source: Molecular Therapy)
Source: Molecular Therapy - September 28, 2016 Category: Genetics & Stem Cells Source Type: research
A Cure For Hemophilia: the Promise Becomes a Reality
Molecular Therapy 24,
1503 (september 2016). doi:10.1038/mt.2016.169
Author: Roland W Herzog (Source: Molecular Therapy)
Source: Molecular Therapy - September 28, 2016 Category: Genetics & Stem Cells Authors: Roland W Herzog Source Type: research
