Safe and Efficient Gene Therapy for Pyruvate Kinase Deficiency
Safe and Efficient Gene Therapy for Pyruvate Kinase Deficiency
Molecular Therapy 24,
1187 (July 2016). doi:10.1038/mt.2016.87
Authors: Maria Garcia-Gomez, Andrea Calabria, Maria Garcia-Bravo, Fabrizio Benedicenti, Penelope Kosinski, Sergio López-Manzaneda, Collin Hill, María del Mar Mañu-Pereira, Miguel A Martín, Israel Orman, Joan-LLuis Vives-Corrons, Charles Kung, Axel Schambach, Shengfang Jin, Juan A Bueren, Eugenio Montini, Susana Navarro & Jose C Segovia
Source: Molecular Therapy - Category: Genetics & Stem Cells Authors: Maria Garcia-Gomez Andrea Calabria Maria Garcia-Bravo Fabrizio Benedicenti Penelope Kosinski Sergio L ópez-Manzaneda Collin Hill Mar ía del Mar Mañu-Pereira Miguel A Mart ín Israel Orman Joan-LLuis Vives-Corrons Charles Kung Axel Schambach Shengfang J Source Type: research