Safe and Efficient Gene Therapy for Pyruvate Kinase Deficiency

Safe and Efficient Gene Therapy for Pyruvate Kinase Deficiency Molecular Therapy 24, 1187 (July 2016). doi:10.1038/mt.2016.87 Authors: Maria Garcia-Gomez, Andrea Calabria, Maria Garcia-Bravo, Fabrizio Benedicenti, Penelope Kosinski, Sergio López-Manzaneda, Collin Hill, María del Mar Mañu-Pereira, Miguel A Martín, Israel Orman, Joan-LLuis Vives-Corrons, Charles Kung, Axel Schambach, Shengfang Jin, Juan A Bueren, Eugenio Montini, Susana Navarro & Jose C Segovia
Source: Molecular Therapy - Category: Genetics & Stem Cells Authors: Source Type: research