Therapy-type related long-term outcomes in mucopolysaccaridosis type II (Hunter syndrome) – Case series

Publication date: September 2021Source: Molecular Genetics and Metabolism Reports, Volume 28Author(s): Mojca Zerjav Tansek, Jana Kodric, Simona Klemencic, Jaap Jan Boelens, Peter M. van Hasselt, Ana Drole Torkar, Maja Doric, Alenka Koren, Simona Avcin, Tadej Battelino, Urh Groselj
Source: Molecular Genetics and Metabolism Reports - Category: Genetics & Stem Cells Source Type: research
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