Open-label phase 1/2 study of vestronidase alfa for mucopolysaccharidosis VII

Publication date: September 2021Source: Molecular Genetics and Metabolism Reports, Volume 28Author(s): Simon Jones, Mahmut Coker, Antonio González-Meneses López, Jennifer Sniadecki, Jill Mayhew, Pauline Hensman, Agnieszka Jurecka
Source: Molecular Genetics and Metabolism Reports - Category: Genetics & Stem Cells Source Type: research
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