Long-term safety and outcomes in hereditary tyrosinaemia type 1 with nitisinone treatment: a 15-year non-interventional, multicentre study

Publication date: Available online 21 May 2021Source: The Lancet Diabetes & EndocrinologyAuthor(s): Ute Spiekerkoetter, Maria L Couce, Anibh M Das, Corinne de Laet, Carlo Dionisi-Vici, Allan M Lund, Manuel Schiff, Marco Spada, Erik Sparve, Johan Szamosi, Roshni Vara, Mattias Rudebeck
Source: The Lancet Diabetes and Endocrinology - Category: Endocrinology Source Type: research