Safety and improved efficacy outcomes in children with aadc deficiency treated with eladocagene exuparvovec gene therapy: results from three clinical trials

Publication date: April 2021Source: Cytotherapy, Volume 23, Issue 4, SupplementAuthor(s): PWL Hwu, PE Pachelli, YH Chien, NC Lee, SH Tseng, CH Tai, AM Conway, A Federhen, L Giugliani, T Felix, M Pykett
Source: Cytotherapy - Category: Cytology Source Type: research