Nonclinical safety evaluation of pabinafusp alfa, an anti-human transferrin receptor antibody and iduronate-2-sulfatase fusion protein, for the treatment of neuronopathic mucopolysaccharidosis type II

Publication date: June 2021Source: Molecular Genetics and Metabolism Reports, Volume 27Author(s): Ryuji Yamamoto, Eiji Yoden, Noboru Tanaka, Masafumi Kinoshita, Atsushi Imakiire, Tohru Hirato, Kohtaro Minami
Source: Molecular Genetics and Metabolism Reports - Category: Genetics & Stem Cells Source Type: research
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