Biochemical evaluation of intracerebroventricular rhNAGLU-IGF2 enzyme replacement therapy in neonatal mice with Sanfilippo B syndrome

Publication date: Available online 31 March 2021Source: Molecular Genetics and MetabolismAuthor(s): Shih-hsin Kan, Ibrahim Elsharkawi, Steven Q. Le, Heather Prill, Linley Mangini, Jonathan D. Cooper, Roger Lawrence, Mark S. Sands, Brett E. Crawford, Patricia I. Dickson
Source: Molecular Genetics and Metabolism - Category: Genetics & Stem Cells Source Type: research