Addition of iptacopan, an oral factor B inhibitor, to eculizumab in patients with paroxysmal nocturnal haemoglobinuria and active haemolysis: an open-label, single-arm, phase 2, proof-of-concept trial

Publication date: Available online 23 March 2021Source: The Lancet HaematologyAuthor(s): Antonio M Risitano, Alexander Röth, Juliette Soret, Camilla Frieri, Flore Sicre de Fontbrune, Luana Marano, Ferras Alashkar, Lina Benajiba, Serena Marotta, Izabela Rozenberg, Julie Milojevic, Peter End, Prasanna K Nidamarthy, Guido Junge, Régis Peffault de Latour

Source: The Lancet Haematology - March 23, 2021 Category: Hematology Source Type: research