Long-term outcomes of patients with mucopolysaccharidosis VI treated with galsulfase enzyme replacement therapy since infancy

Publication date: Available online 14 March 2021Source: Molecular Genetics and MetabolismAuthor(s): Paula Garcia, Dawn Phillips, JoAnn Johnson, Kenneth Martin, Linda M. Randolph, Howard Rosenfeld, Paul Harmatz

Source: Molecular Genetics and Metabolism - March 15, 2021 Category: Genetics & Stem Cells Source Type: research