Real-world data assessment of safety of home-based and hospital/outpatient-based laronidase enzyme replacement therapy for mucopolysaccharidosis I

Publication date: Available online 4 March 2021Source: Molecular Genetics and Metabolism ReportsAuthor(s): Amanda Wilson, Raffaella M. Colzani, Ana Lorena Flores

Source: Molecular Genetics and Metabolism Reports - March 5, 2021 Category: Genetics & Stem Cells Source Type: research