Long-term impact of early initiation of enzyme replacement therapy in 34 MPS VI patients: A resurvey study

Publication date: Available online 27 February 2021Source: Molecular Genetics and MetabolismAuthor(s): Dafne D.G. Horovitz, Emília K.E.A. Leão, Erlane M. Ribeiro, Ana M. Martins, Anneliese L. Barth, João I.C.F. Neri, Marcelo Kerstenetzky, Ana C.M. Siqueira, Bethania F.R. Ribeiro, Chong A. Kim, Francisca C. Santos, José F.S. Franco, Leniza C.L. Lichtvan, Liane R. Giuliani, Maria Do C.S. Rodrigues, Renata C.F. Bonatti, Thaís B. Teixeira, Alexandra Gonçalves, Charles M. Lourenço, Ane S.S. Pereira

Source: Molecular Genetics and Metabolism - February 27, 2021 Category: Genetics & Stem Cells Source Type: research