Standardising clinical outcomes measures for adult clinical trials in Fabry disease: A global Delphi consensus

Publication date: Available online 20 February 2021Source: Molecular Genetics and MetabolismAuthor(s): D. Moreno-Martinez, P. Aguiar, C. Auray-Blais, M. Beck, D.G. Bichet, A. Burlina, D. Cole, P. Elliott, U. Feldt-Rasmussen, S. Feriozzi, J. Fletcher, R. Giugliani, A. Jovanovic, C. Kampmann, M. Langeveld, O. Lidove, A. Linhart, M. Mauer, J.C. Moon, A. Muir
Source: Molecular Genetics and Metabolism - Category: Genetics & Stem Cells Source Type: research