Generation of a gene-corrected isogenic iPSC line (AHQUi001-A-1) from a patient with familial hypertriglyceridemia (FHTG) carrying a heterozygous p.C310R (c.928 T > C) mutation in LPL gene using CRISPR/Cas9

Publication date: April 2021Source: Stem Cell Research, Volume 52Author(s): Xiaofang Sun, Xiang Zhou, Bingzi Dong, Chen Wang, Xinhua Xiao, Yangang Wang
Source: Stem Cell Research - Category: Stem Cells Source Type: research