Clinical outcomes in a series of 18 patients with long chain fatty acids oxidation disorders treated with triheptanoin for a median duration of 22 months

Publication date: Available online 10 February 2021Source: Molecular Genetics and MetabolismAuthor(s): Nathalie Guffon, Fanny Mochel, Manuel Schiff, Pascale De Lonlay, Claire Douillard, Christine Vianey-Saban

Source: Molecular Genetics and Metabolism - February 11, 2021 Category: Genetics & Stem Cells Source Type: research