Open-label clinical trial of anakinra in mucopolysaccharidosis type III: Interim analysis

Publication date: February 2021Source: Molecular Genetics and Metabolism, Volume 132, Issue 2Author(s): Lynda E. Polgreen, Agnes Chen, Cara O'Neill, Anna Luzzi, Michelina Iacovino, Julie Eisengart
Source: Molecular Genetics and Metabolism - Category: Genetics & Stem Cells Source Type: research