A qualitative study of the experience of venglustat for patients with Gaucher disease type 3 (GD3) in LEAP: A phase II open-label, multicenter, multinational study

Publication date: February 2021Source: Molecular Genetics and Metabolism, Volume 132, Issue 2Author(s): Camille Rochmann, James Turnbull, Robert Krupnick, Chad Gwaltney, Ruth Pulikotil-Jacob, Ali Hariri, Alaa Hamed
Source: Molecular Genetics and Metabolism - Category: Genetics & Stem Cells Source Type: research