In utero enzyme replacement therapy in fetuses with lysosomal diseases: A phase I clinical trial

Publication date: February 2021Source: Molecular Genetics and Metabolism, Volume 132, Issue 2Author(s): Marisa E. Schwab, Jennifer L. Cohen, Billie Lianoglou, Renata C. Gallagher, Juan M. Gonzalez-Velez, Teresa N. Sparks, Mary E. Norton, Michael H. Gelb, Tim Wood, Priya S. Kishnani, Paul R. Harmatz, Tippi C. MacKenzie
Source: Molecular Genetics and Metabolism - Category: Genetics & Stem Cells Source Type: research