Non-clinical evaluation of a blood-brain barrier-penetrable N-sulfoglucosamine sulfohydrolase in a mouse model of mucopolysaccharidosis type IIIA

Publication date: February 2021Source: Molecular Genetics and Metabolism, Volume 132, Issue 2Author(s): Satowa Tanaka, Sachiho Kida, Yuri Koshimura, Shinji Kakimoto, Atsushi Imakiire, Jun Ito, Kazuki Miyauchi, Hideto Morimoto, Kohtaro Minami, Tohru Hirato, Hiroyuki Sonoda
Source: Molecular Genetics and Metabolism - Category: Genetics & Stem Cells Source Type: research
More News: Brain | Genetics | Neurology