AVR-RD-01, an investigational lentiviral gene therapy for Fabry disease: Overview of clinical data from phase 1 and phase 2 studies

Publication date: February 2021Source: Molecular Genetics and Metabolism, Volume 132, Issue 2Author(s): Mark Thomas, Kathleen Nicholls, Benedict Carnley, Mirjam Trame, Chris Mason, Fatemeh Tavakkoli, Greg Keenan

Source: Molecular Genetics and Metabolism - February 2, 2021 Category: Genetics & Stem Cells Source Type: research