Two siblings with attenuated MPS II form: Long term enzyme replacement therapy

Publication date: February 2021Source: Molecular Genetics and Metabolism, Volume 132, Issue 2Author(s): Nato Vashakmadze, Leyla Namazova-Baranova, Natalia Zhurkova, Olga Gordeeva, Nina Fedorova, Georgii Karkashadze, Elena Komarova, Kirill Savostianov, Kirill Savostianov, Aleksandr Pushkov
Source: Molecular Genetics and Metabolism - Category: Genetics & Stem Cells Source Type: research
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