Development of a novel gene therapy for Fabry disease: Engineered alpha-galactosidase A transgene for improved stability

Publication date: February 2021Source: Molecular Genetics and Metabolism, Volume 132, Issue 2Author(s): Tobias Willer, Juliette Hordeaux, Pai-Chi Tsai, Daniel Ellsworth, Su Xu, Helen Eisenach, Jinsong Shen, Jean-Pierre Louboutin, Peter Bell, Chunjuan Song, Quyen Q. Hoang, Russell Gotschall, Jill Weimer, James M. Wilson, Hung Do

Source: Molecular Genetics and Metabolism - February 2, 2021 Category: Genetics & Stem Cells Source Type: research