Caregiver experiences of intrathecal idursulfase-IT treatment in pediatric patients with neuronopathic mucopolysaccharidosis type II

Publication date: February 2021Source: Molecular Genetics and Metabolism, Volume 132, Issue 2Author(s): Karen S. Yee, Sandy Lewis, Emily Evans, Carla Romano, David Alexanderian
Source: Molecular Genetics and Metabolism - Category: Genetics & Stem Cells Source Type: research