Limitations and Challenges of Conducting Budget Impact Analyses in Rare Diseases: A Case Study of Alpha-1 Antitrypsin Deficiency

Publication date: December 2020Source: Value in Health Regional Issues, Volume 23Author(s): Juan-David Rueda, Jan Sieluk, Robert A. Sandhaus, C. Daniel Mullins
Source: Value in Health Regional Issues - Category: International Medicine & Public Health Source Type: research