Therapy development for the mucopolysaccharidoses: Updated consensus recommendations for neuropsychological endpoints

Publication date: Available online 31 August 2020Source: Molecular Genetics and MetabolismAuthor(s): Johanna H. van der Lee, Jonathan Morton, Heather R. Adams, Lorne Clarke, Julie B. Eisengart, Maria L. Escolar, Roberto Giugliani, Paul Harmatz, Melissa Hogan, Shauna Kearney, Joseph Muenzer, Nicole Muschol, Stewart Rust, Benjamin R. Saville, Margaret Semrud-Clikeman, Raymond Wang, Elsa Shapiro
Source: Molecular Genetics and Metabolism - Category: Genetics & Stem Cells Source Type: research