Long-term efficacy and safety of migalastat treatment in Fabry disease: 30-month results from the open-label extension of the randomized, phase 3 ATTRACT study

Publication date: Available online 15 August 2020Source: Molecular Genetics and MetabolismAuthor(s): Ulla Feldt-Rasmussen, Derralynn Hughes, Gere Sunder-Plassmann, Suma Shankar, Khan Nedd, Iacopo Olivotto, Damara Ortiz, Toya Ohashi, Takashi Hamazaki, Nina Skuban, Julie Yu, Jay A. Barth, Kathleen Nicholls

Source: Molecular Genetics and Metabolism - August 17, 2020 Category: Genetics & Stem Cells Source Type: research