Mutation-Specific Guide RNA for Compound Heterozygous Porphyria On-target Scarless Correction by CRISPR/Cas9 in Stem Cells

Publication date: Available online 13 August 2020Source: Stem Cell ReportsAuthor(s): Florence Prat, Jérôme Toutain, Julian Boutin, Samuel Amintas, Grégoire Cullot, Magalie Lalanne, Isabelle Lamrissi-Garcia, Isabelle Moranvillier, Emmanuel Richard, Jean-Marc Blouin, Sandrine Dabernat, François Moreau-Gaudry, Aurélie Bedel
Source: Stem Cell Reports - Category: Stem Cells Source Type: research