An online survey of burden of illness in families with mucopolysaccharidosis type II children in the United States

Publication date: December 2019Source: Molecular Genetics and Metabolism Reports, Volume 21Author(s): Therese Conner, Francesca Cook, Vivian Fernandez, Vanessa Rangel-Miller
Source: Molecular Genetics and Metabolism Reports - Category: Genetics & Stem Cells Source Type: research