Considerations for evaluating the effectiveness and long term outcome of enzyme replacement therapy in Pompe disease.

Considerations for evaluating the effectiveness and long term outcome of enzyme replacement therapy in Pompe disease.
Korean J Pediatr. 2019 Aug 07;:
Authors: Cheon CK
PMID: 31401827 [PubMed - as supplied by publisher]

Source: Korean Journal of Pediatrics - August 14, 2019 Category: Pediatrics Tags: Korean J Pediatr Source Type: research