A Phase 1 healthy male volunteer single escalating dose study of the pharmacokinetics and pharmacodynamics of risdiplam (RG7916, RO7034067), a SMN2 splicing modifier
British Journal of Clinical Pharmacology,Volume 0, Issue ja, -Not available-.
Source: British Journal of Clinical Pharmacology - Category: Drugs & Pharmacology Authors: Stefan Sturm,
Andreas G ünther,
Birgit Jaber,
Paul Jordan,
Nada Al Kotbi,
Nikhat Parkar,
Yumi Cleary,
Nicolas Frances,
Tobias Bergauer,
Katja Heinig,
Heidemarie Kletzl,
Anne Marquet,
Hasane Ratni,
Agnès Poirier,
Lutz Müller,
Christian Cz Source Type: research