International differences in patient access to ultra-orphan drugs

ConclusionsLarge differences in patient access to ultra-orphan drugs were observed between countries. Future research should examine if similar findings can be seen in other countries and with other orphan drugs, and it should also determine which other factors play a role in reimbursement status of orphan drugs.

Source: Health Policy and Technology - July 10, 2018 Category: Health Management Source Type: research