The use of lumacaftor/ivacaftor to treat acute deterioration in paediatric cystic fibrosis

We describe the use of this drug to treat a child with an unusually severe exacerbation of CF lung disease and review the potential of lumacaftor/ivacaftor as a rescue therapy in the paediatric CF population.
Source: Paediatric Respiratory Reviews - Category: Respiratory Medicine Authors: Tags: The 2017 Royal Society Of Medicine Cystic Fibrosis Symposium Source Type: research