Long ‐term clinical and economic outcomes in previously untreated paediatric patients with severe haemophilia A: A nationwide real‐world study with 700 person‐years

ConclusionsEarly high‐dose prophylaxis leads to excellent long‐term clinical outcomes, and early childhood ITI therapy seems to turn cost‐neutral generally already in 2 years.

http://onlinelibrary.wiley.com/resolve/doi?DOI=10.1111%2Fhae.13447

Source: Haemophilia - March 1, 2018 Category: Hematology Authors: K. Veps äläinen, P. Riikonen, R. Lassila, M. Arola, P. Huttunen, P. Lähteenmäki, M. Möttönen, T. Selander, J. Martikainen Tags: ORIGINAL ARTICLE Source Type: research