Adeno‐associated virus 8‐mediated gene therapy for choroideremia: preclinical studies in in vitro and in vivo models

ConclusionsAAV8 is a promising vector for human clinical gene therapy trials for choroideremia. Copyright © 2014 John Wiley & Sons, Ltd.

Source: The Journal of Gene Medicine - July 21, 2014 Category: Genetics & Stem Cells Authors: Aaron Black, Vidyullatha Vasireddy, Daniel C. Chung, Albert M. Maguire, Rajashekhar Gaddameedi, Tania Tolmachova, Miguel Seabra, Jean Bennett Tags: Research Article Source Type: research