FDA OKs first in vitro route to expanded approval

Nature Reviews Drug Discovery 16, 591 (2017). doi:10.1038/nrd.2017.140 Author: Katie Kingwell In vitro data can be used to accelerate the approval of drugs that target specific disease-causing mutations for additional subpopulations of patients with rare diseases such as cystic fibrosis.
Source: Nature Reviews Drug Discovery - Category: Drugs & Pharmacology Authors: Tags: News and Analysis Source Type: research