Nine paths to PCSK9 inhibition

Nature Reviews Drug Discovery 16, 299 (2017). doi:10.1038/nrd.2017.83 Author: Asher Mullard A lipid-modulating protein that exemplifies the value of human genetics for target validation has provided a fertile testing ground for new drug modalities including long-acting RNA interference drugs, vaccines against self-antigens, CRISPR therapeutics and small molecules that control ribosomal activity.
Source: Nature Reviews Drug Discovery - Category: Drugs & Pharmacology Authors: Tags: News and Analysis Source Type: research