Gene Therapy for Achromatopsia

ConclusionDuring the last years, huge progress has been made towards bringing a curative treatment for ACHM into clinics. First clinical trials are ongoing or will be launched soon and are expected to contribute important data on the safety and efficacy of ACHM gene supplementation therapy.

Source: The Journal of Gene Medicine - October 31, 2016 Category: Genetics & Stem Cells Authors: Stylianos Michalakis, Christian Sch ön, Elvir Becirovic, Martin Biel Tags: REVIEW ARTICLE Source Type: research