Low-dose Gene Therapy Reduces the Frequency of Enzyme Replacement Therapy in a Mouse Model of Lysosomal Storage Disease
Low-dose Gene Therapy Reduces the Frequency of Enzyme Replacement Therapy in a Mouse Model of Lysosomal Storage Disease
Molecular Therapy 24,
2054 (December 2016). doi:10.1038/mt.2016.181
Authors: Marialuisa Alliegro, Rita Ferla, Edoardo Nusco, Chiara De Leonibus, Carmine Settembre & Alberto Auricchio
Source: Molecular Therapy - Category: Genetics & Stem Cells Authors: Marialuisa Alliegro Rita Ferla Edoardo Nusco Chiara De Leonibus Carmine Settembre Alberto Auricchio Source Type: research
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