AAV-mediated gene therapy in Dystrophin-Dp71 deficient mouse leads to blood-retinal barrier restoration and oedema reabsorption

This study is the basis for the development of new therapeutic strategies in dealing with diseases with BRB breakdown and macular oedema such as diabetic retinopathy (DR).

Source: Human Molecular Genetics - November 27, 2016 Category: Genetics & Stem Cells Authors: Vacca, O., Charles-Messance, H., El Mathari, B., Sene, A., Barbe, P., Fouquet, S., Aragon, J., Darche, M., Giocanti-Auregan, A., Paques, M., Sahel, J.-A., Tadayoni, R., Montanez, C., Dalkara, D., Rendon, A. Tags: ARTICLES Source Type: research