Morpholino-mediated Knockdown of DUX4 Toward Facioscapulohumeral Muscular Dystrophy Therapeutics

Morpholino-mediated Knockdown of DUX4 Toward Facioscapulohumeral Muscular Dystrophy Therapeutics Molecular Therapy 24, 1405 (August 2016). doi:10.1038/mt.2016.111 Authors: Jennifer CJ Chen, Oliver D King, Yuanfan Zhang, Nicholas P Clayton, Carrie Spencer, Bruce M Wentworth, Charles P Emerson & Kathryn R Wagner
Source: Molecular Therapy - Category: Genetics & Stem Cells Authors: Source Type: research