rAAV Gene Therapy in a Canavan’s Disease Mouse Model Reveals Immune Impairments and an Extended Pathology Beyond the Central Nervous System
rAAV Gene Therapy in a Canavan’s Disease Mouse Model Reveals Immune Impairments and an Extended Pathology Beyond the Central Nervous System
Molecular Therapy 24,
1030 (June 2016). doi:10.1038/mt.2016.68
Authors: Seemin Seher Ahmed, Stefan A Schattgen, Ashley E Frakes, Elif M Sikoglu, Qin Su, Jia Li, Thomas G Hampton, Andrew R Denninger, Daniel A Kirschner, Brian Kaspar, Reuben Matalon & Guangping Gao
Source: Molecular Therapy - Category: Genetics & Stem Cells Authors: Seemin Seher AhmedStefan A SchattgenAshley E FrakesElif M SikogluQin SuJia LiThomas G HamptonAndrew R DenningerDaniel A KirschnerBrian KasparReuben MatalonGuangping Gao Source Type: research