AAV-mediated Gene Therapy Halts Retinal Degeneration in PDE6β-deficient Dogs

AAV-mediated Gene Therapy Halts Retinal Degeneration in PDE6β-deficient Dogs Molecular Therapy 24, 867 (May 2016). doi:10.1038/mt.2016.37 Authors: Virginie Pichard, Nathalie Provost, Alexandra Mendes-Madeira, Lyse Libeau, Philippe Hulin, Kizito-Tshitoko Tshilenge, Marine Biget, Baptiste Ameline, Jack-Yves Deschamps, Michel Weber, Guylène Le Meur, Marie-Anne Colle, Philippe Moullier & Fabienne Rolling
Source: Molecular Therapy - Category: Genetics & Stem Cells Authors: Source Type: research
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