Sleeping Beauty Transposon Vectors in Liver-directed Gene Delivery of LDLR and VLDLR for Gene Therapy of Familial Hypercholesterolemia

Sleeping Beauty Transposon Vectors in Liver-directed Gene Delivery of LDLR and VLDLR for Gene Therapy of Familial Hypercholesterolemia Molecular Therapy 24, 620 (March 2016). doi:10.1038/mt.2015.221 Authors: Tytteli A K Turunen, Jere Kurkipuro, Tommi Heikura, Taina Vuorio, Elisa Hytönen, Zsuzsanna Izsvák & Seppo Ylä-Herttuala
Source: Molecular Therapy - Category: Genetics & Stem Cells Authors: Source Type: research