CRISPR/dCas9-mediated Transcriptional Inhibition Ameliorates the Epigenetic Dysregulation at D4Z4 and Represses DUX4-fl in FSH Muscular Dystrophy
CRISPR/dCas9-mediated Transcriptional Inhibition Ameliorates the Epigenetic Dysregulation at D4Z4 and Represses DUX4-fl in FSH Muscular Dystrophy
Molecular Therapy 24,
527 (March 2016). doi:10.1038/mt.2015.200
Authors: Charis L Himeda, Takako I Jones & Peter L Jones
Source: Molecular Therapy - Category: Genetics & Stem Cells Authors: Charis L HimedaTakako I JonesPeter L Jones Source Type: research