CRISPR/dCas9-mediated Transcriptional Inhibition Ameliorates the Epigenetic Dysregulation at D4Z4 and Represses DUX4-fl in FSH Muscular Dystrophy

CRISPR/dCas9-mediated Transcriptional Inhibition Ameliorates the Epigenetic Dysregulation at D4Z4 and Represses DUX4-fl in FSH Muscular Dystrophy Molecular Therapy 24, 527 (March 2016). doi:10.1038/mt.2015.200 Authors: Charis L Himeda, Takako I Jones & Peter L Jones
Source: Molecular Therapy - Category: Genetics & Stem Cells Authors: Source Type: research